The Management of Patients with Rare Diseases Resource Center contains a compilation of resources that pharmacy professionals may find helpful for …
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Developing their understanding of rare disorders (any disease, disorder, illness or condition affecting fewer than 200K people in the US is considered rare)
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Expanding their knowledge base of rare disease resources (common disease states and resources are well known, resources related to rare diseases are less known)
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Keeping up-to-date on new drug developments and orphan drug products within the specialty (more than 90% of rare diseases are without an FDA-approved treatment)
